FDA proposes new treatment approval pathway for ultrarare diseases

FDA proposes new treatment approval pathway for ultrarare diseases

Health Care News – Read More The Food and Drug Administration (FDA) announced a new proposal Monday for flexible drug approval pathway treatments addressing ultrarare diseases. The FDA unveiled draft guidance on a proposed regulatory pathway for individualized therapies, treatments for rare conditions that affect a very small population, with the proposal specifically focusing on genome editing and RNA-based therapies. The… 

CDC No. 2 steps down amid HHS shake-up

CDC No. 2 steps down amid HHS shake-up

Blood test could predict when Alzheimer’s symptoms will begin

Blood test could predict when Alzheimer’s symptoms will begin